Treatment
These are treatment programs under investigation, not established treatment options. Each record links to the separate Research study record when available.
Treatment records
3 sourced records.
INVESTIGATIONAL
Brand / formulation: Qalsody (investigational use outside the approved SOD1 indication)
A study program evaluating tofersen outside its FDA-approved SOD1-ALS indication.
INVESTIGATIONAL
An oral investigational treatment being evaluated in the PREVAiLS Phase 3 ALS study.
INVESTIGATIONAL
An oral investigational treatment being evaluated in the UNITE-ALS study.
Sources & Further Reading
These source cards link directly to the original material. External websites open in a new tab.
Mayo Clinic
A direct source for reviewing the medical, genetic, research, or policy information discussed on this page.
Retrieved: Not stated · Last verified: 09-30-2026
Previous: Not stated
New: Not stated
American Academy of Neurology / PubMed Central
Evidence review covering multidisciplinary ALS care, symptoms, communication, nutrition, respiratory care, and comfort.
Visit sourceTreatment information is provided for education and navigation and does not replace medical advice. Whether a treatment is appropriate depends on the individual’s diagnosis, genetic status, symptoms, health status, and other clinical factors. Treatment decisions should be made with the person’s ALS care team.
Treatment records last verified: 09-30-2026